Investigators at Boston institutions believe the regimen could target immunosuppressive lipid macrophages and improve ...

A sponsor will have to demonstrate success with "with several consecutive patients with different bespoke therapies" to ...

Studies of germline genetic testing programs provide a snapshot of challenges at academic and community practices at the NSGC annual meeting.

CTX310 showed promising safety and efficacy in a small Phase I trial, according to data presented at the American Heart ...

The agency reviewed data from a Phase II study, in which around 21 percent of patients had a complete response to the menin inhibitor.

NEW YORK – Fondazione Telethon said Friday that the European Medicines Agency's Committee for Medicinal Products for Human Use (CHMP) has recommended marketing authorization for its gene therapy ...

The agency is cautioning patients about the risk of serious, possibly fatal, liver injuries and has limited the gene therapy's use to ambulatory patients.

The committee reviewed data from studies showing that the antisense oligonucleotide reduced the monthly mean rate of angioedema attacks.

At its annual meeting, the society discussed progress it has made in pushing ahead the Access to Genetic Counselor Services ...

NEW YORK – German biotech ITM Isotope Technologies Munich has submitted a new drug application to the US Food and Drug Administration for its radiopharmaceutical 177Lu-edotreotide as a treatment for ...