The blood creatinine-to-cystatin-c ratio may be a biomarker of Spinraza treatment response in children with SMA, a study in ...

Columnist Sherry Toh writes of her love for Disney's "Beauty and the Beast" and reimagines a production led by a person with a disability.

At first, columnist Connie Chandler wasn't sold on the idea of attending a global prom. But she was soon convinced it's a ...

Researchers described what they believe to be the first case of SMA type 4 presenting with a false enlargement of a muscle in ...

After a year of struggling to fill his home health nursing positions, things are turning around for columnist.

The strength of nerve electrical impulses in children with SMA can help predict their response to treatment with Spinraza, a study found.

Treatment with a high-dose regimen of Spinraza safely improved motor function in children with SMA, according to data from ...

Columnist Jasmine Ramos explains her complicated feelings surrounding widespread coverage of a celebrity's SMA diagnosis ...

Women with spinal muscular atrophy (SMA) can experience successful pregnancies and give birth to healthy babies when ...

A test using a zebrafish model helped clinicians rule out SMA in two children, showing its potential use to clarify genetic ...

As a genetic disorder that causes progressive muscle weakness and wasting, spinal muscular atrophy (SMA) can pose challenges to everyday life. However, many people living with SMA find ways to adapt, ...

What is Spinraza for SMA? Spinraza (nusinersen) is an injection therapy widely approved for treating adults and children with spinal muscular atrophy (SMA). It was the first therapy approved to target ...